Low-income foundations focusing on rare diseases should have the same scientific support and opportunities as other larger organizations that can afford a considerable investment in research and drug discovery strategy.
finding a cure, where to start
To accelerate the development of appropriate therapeutics in your disease.Understand the process of drug discovery and development.
Perform analysisof research status, gap identification in your disease area.
Build a roadmapto pharmafor your specific fields by providing comprehensible scientific and strategic advice.
Gatherstakeholders, government, industry and academic support. Use the help from umbrella organizations.
Plan for Rare foundation educates and guides young rare and ultra-rare disease foundations in the process to get to drug development. We prepare them to identify and get the appropriate pre-clinical and clinical tools to be ready to interact properly with the FDA and the biotech/pharmaceutical industry.
Young low-income foundations often don’t know where to start besides helping to their best the few scientists and doctors they know in the field of their disease. The foundations' goals are primarily to find a cure but lack the knowledge of drug discovery readiness, and at times, the basic scientists they work with genuinely don’t know either.
We help the foundations with performing a landscape analysis so they can be ready for translating great science into patient benefit.
We want to bring specially designed toolboxes to them, including:
Interaction-collaboration toolbox(understand the process, who are the stakeholders, when to start interacting, establish a balanced portfolio).
Preclinical toolbox (cellular models, appropriate animal models, cellular assays compatible with middle to high throughput screening).
Clinical toolbox(natural history, endpoints, standardization of measures, any type of registry).
Expansion toolbox (expansion to other rare diseases with similar mechanisms and/or endpoints, interactions with foundations from other continents).
Partnering to go faster
Andrea Taylor, President/Founder of A Twist of Fate-ATS and Jade Day, vice-president are partnering with Armelle Pindon, President of Plan4Rare for a better strategy in Arterial Tortuosity Syndrome.
Network & Accreditation